CRISPR Gene Therapy Cures Sickle Cell Disease in 100 Patients
CRISPR gene therapy has cured sickle cell disease in all 100 patients treated in an expanded trial. The one-time treatment permanently corrects the genetic defect, eliminating the need for lifelong blood transfusions.
CRISPR cures sickle cell
100% Success Rate
All 100 patients in the expanded trial have been cured of sickle cell disease with no disease recurrence after up to four years of follow-up. Patients report dramatic improvements in quality of life.
Treatment Process
Stem cells are removed from patients, edited using CRISPR to correct the sickle cell mutation, then returned. The corrected cells proliferate, producing healthy hemoglobin.
Global Impact
Sickle cell affects millions worldwide, primarily in Africa and among African diaspora populations. The challenge now is making the expensive treatment accessible globally.
CRISPR gene therapy has cured sickle cell disease in 100 patients, offering a permanent solution that eliminates the need for lifelong blood transfusions.
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